Browsing Diğer Yayınlar Koleksiyonu by Publisher "Elsevier Science Ltd"
Now showing items 1-1 of 1
-
Evaluation of the therapeutic efficacy and tolerability of current drug treatments on the clinical outcomes of paediatric spinal muscular atrophy type 1: A systematic review
(Elsevier Science Ltd, 2023)Spinal muscular atrophy (SMA) is a severe hereditary lower motor neuron disorder characterised by degeneration of alpha motor neurons in the spinal cord, resulting in progressive weakness and paralysis of proximal muscles. ...